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CA2602730A1 - Defective sindbis viral vectors - Google Patents

Defective sindbis viral vectors Download PDF

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Publication number
CA2602730A1
CA2602730A1 CA002602730A CA2602730A CA2602730A1 CA 2602730 A1 CA2602730 A1 CA 2602730A1 CA 002602730 A CA002602730 A CA 002602730A CA 2602730 A CA2602730 A CA 2602730A CA 2602730 A1 CA2602730 A1 CA 2602730A1
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Canada
Prior art keywords
seq
nucleotide sequence
set forth
mut
defective sindbis
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CA002602730A
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French (fr)
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CA2602730C (en
Inventor
Alicia Hurtado
Daniel Meruelo
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New York University NYU
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    • C12N7/00Viruses; Bacteriophages; Compositions thereof; Preparation or purification thereof
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61KPREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K35/00Medicinal preparations containing materials or reaction products thereof with undetermined constitution
    • A61K35/66Microorganisms or materials therefrom
    • A61K35/76Viruses; Subviral particles; Bacteriophages
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61PSPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P35/00Antineoplastic agents
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61PSPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P35/00Antineoplastic agents
    • A61P35/02Antineoplastic agents specific for leukemia
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61PSPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P43/00Drugs for specific purposes, not provided for in groups A61P1/00-A61P41/00
    • CCHEMISTRY; METALLURGY
    • C07ORGANIC CHEMISTRY
    • C07KPEPTIDES
    • C07K14/00Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof
    • C07K14/005Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof from viruses
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    • C12N15/00Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor
    • C12N15/09Recombinant DNA-technology
    • C12N15/63Introduction of foreign genetic material using vectors; Vectors; Use of hosts therefor; Regulation of expression
    • C12N15/79Vectors or expression systems specially adapted for eukaryotic hosts
    • C12N15/85Vectors or expression systems specially adapted for eukaryotic hosts for animal cells
    • C12N15/86Viral vectors
    • AHUMAN NECESSITIES
    • A01AGRICULTURE; FORESTRY; ANIMAL HUSBANDRY; HUNTING; TRAPPING; FISHING
    • A01KANIMAL HUSBANDRY; AVICULTURE; APICULTURE; PISCICULTURE; FISHING; REARING OR BREEDING ANIMALS, NOT OTHERWISE PROVIDED FOR; NEW BREEDS OF ANIMALS
    • A01K2267/00Animals characterised by purpose
    • A01K2267/03Animal model, e.g. for test or diseases
    • A01K2267/0331Animal model for proliferative diseases
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    • C12BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
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    • C12N2770/00MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA ssRNA viruses positive-sense
    • C12N2770/00011Details
    • C12N2770/36011Togaviridae
    • C12N2770/36111Alphavirus, e.g. Sindbis virus, VEE, EEE, WEE, Semliki
    • C12N2770/36122New viral proteins or individual genes, new structural or functional aspects of known viral proteins or genes
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    • C12N2770/00MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA ssRNA viruses positive-sense
    • C12N2770/00011Details
    • C12N2770/36011Togaviridae
    • C12N2770/36111Alphavirus, e.g. Sindbis virus, VEE, EEE, WEE, Semliki
    • C12N2770/36132Use of virus as therapeutic agent, other than vaccine, e.g. as cytolytic agent
    • CCHEMISTRY; METALLURGY
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    • C12N2770/00MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA ssRNA viruses positive-sense
    • C12N2770/00011Details
    • C12N2770/36011Togaviridae
    • C12N2770/36111Alphavirus, e.g. Sindbis virus, VEE, EEE, WEE, Semliki
    • C12N2770/36141Use of virus, viral particle or viral elements as a vector
    • C12N2770/36143Use of virus, viral particle or viral elements as a vector viral genome or elements thereof as genetic vector
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    • C12N2770/00MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA ssRNA viruses positive-sense
    • C12N2770/00011Details
    • C12N2770/36011Togaviridae
    • C12N2770/36111Alphavirus, e.g. Sindbis virus, VEE, EEE, WEE, Semliki
    • C12N2770/36161Methods of inactivation or attenuation
    • CCHEMISTRY; METALLURGY
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    • C12N2840/00Vectors comprising a special translation-regulating system
    • C12N2840/20Vectors comprising a special translation-regulating system translation of more than one cistron
    • C12N2840/203Vectors comprising a special translation-regulating system translation of more than one cistron having an IRES

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  • Engineering & Computer Science (AREA)
  • Medicinal Chemistry (AREA)
  • Bioinformatics & Cheminformatics (AREA)
  • Wood Science & Technology (AREA)
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  • General Engineering & Computer Science (AREA)
  • Biotechnology (AREA)
  • Biomedical Technology (AREA)
  • Microbiology (AREA)
  • Pharmacology & Pharmacy (AREA)
  • Veterinary Medicine (AREA)
  • Animal Behavior & Ethology (AREA)
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  • Biophysics (AREA)
  • Molecular Biology (AREA)
  • General Chemical & Material Sciences (AREA)
  • Chemical Kinetics & Catalysis (AREA)
  • Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
  • Gastroenterology & Hepatology (AREA)
  • Physics & Mathematics (AREA)
  • Epidemiology (AREA)
  • Immunology (AREA)
  • Plant Pathology (AREA)
  • Mycology (AREA)
  • Proteomics, Peptides & Aminoacids (AREA)
  • Oncology (AREA)
  • Hematology (AREA)
  • Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
  • Medicines Containing Material From Animals Or Micro-Organisms (AREA)

Abstract

Disclosed herein are new defective Sindbis viral vectors made from wild type Ar-339 Sindbis virus, with differences in replicase and envelope proteins between JT vectors and consensus Sindbis virus sequences, and also between JT
and Ar-339 vectors. Also disclosed are plasmids used for the production of the vectors, methods for producing the vectors, methods for treating mammals suffering from tumors and pharmaceutical formulations for use in the treatment methods.

Claims (15)

1. A purified, isolated nucleic acid coinprising a nucleotide sequence as set forth in SEQ ID
NO.37 (SP6-H).
2. A purified, isolated nucleic acid comprising a nucleotide sequence as set forth in SEQ ID
NO.38 (SP6-H-K70).
3. A purified, isolated nucleic acid comprising a nucleotide sequence as set forth in SEQ ID
NO.40 (SP6-H-K70-V251).
4. A purified, isolated nucleic acid comprising a nucleotide sequence as set forth in SEQ ID
NO:39 (SP6-H-13-K70-E181-Val 251).
5. A purified isolated nucleic acid comprising a nucleotide sequence as set forth in SEQ ID NO:
36 (SP6-R).
6. A method for producing defective Sindbis viral vectors comprising the steps of (a) providing a linearized replicon plasmid comprising the nucleotide sequence as set forth in SEQ ID NO: 36 and a linearized Helper plasmid selected from SEQ ID
NO:
37, SEQ ID NO: 38, SEQ ID NO: 40 and SEQ ID NO: 39;
(b) transcribing said replicon plasmid and one Helper plasmid to produce RNA;
(c) collecting the RNA transcribed in step (b) and transfecting cells with said RNA;
(d) incubating said transfected cells for a time and at a temperature effective for producing defective Sindbis viral vectors; and (e) collecting said defective Sindbis viral vectors from the medium of said transfected cells.
7. The method of claim 6 wherein said Helper plasmid comprises the nucleotide sequence as set forth in SEQ ID NO: 38.
8. The method of claim 6 wherein said Helper plasmid comprises the nucleotide sequence as set forth in SEQ ID NO: 40.
9. The method of claim 6 wherein said Helper plasmid comprises the nucleotide sequence as set forth in SEQ ID NO: 39.
10. The method of claim 6 wherein said Helper plasmid comprises the nucleotide sequence as set forth in SEQ ID NO: 37.
11. A defective Sindbis viral vector produced by the method of claim 6.
12. The defective Sindbis vector of claim 11 wherein said vector is selected from Mut-1, Mut-2 and Mut-4.
13. The method of claim 6 wherein said cell is selected from BHK-21, ES-2, ES-2/Fluc and MOSEC cells.
14. A method for treating a mammal suffering from a tumor comprising administering to a mammal in need of such treatment a therapeutically effective amount of a defective Sindbis viral vector selected from Vector C, Mut-1, Mut-2 and Mut-4.
15. A pharmaceutical formulation for treating a mammal suffering from a tumor comprising a defective Sindbis viral vector selected from Vector C, Mut-1, Mut-2 and Mut-4 and a pharmaceutically acceptable carrier or diluent.
CA2602730A 2005-03-29 2006-03-29 Defective sindbis viral vectors Expired - Fee Related CA2602730C (en)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US66643205P 2005-03-29 2005-03-29
US60/666,432 2005-03-29
US75542805P 2005-12-30 2005-12-30
US60/755,428 2005-12-30
PCT/US2006/011617 WO2006105279A2 (en) 2005-03-29 2006-03-29 Defective sindbis viral vectors

Publications (2)

Publication Number Publication Date
CA2602730A1 true CA2602730A1 (en) 2006-10-05
CA2602730C CA2602730C (en) 2012-03-27

Family

ID=37054122

Family Applications (1)

Application Number Title Priority Date Filing Date
CA2602730A Expired - Fee Related CA2602730C (en) 2005-03-29 2006-03-29 Defective sindbis viral vectors

Country Status (8)

Country Link
US (4) US7303898B2 (en)
EP (1) EP1871425B1 (en)
JP (1) JP4729615B2 (en)
AU (1) AU2006230354B2 (en)
CA (1) CA2602730C (en)
IL (1) IL186234A (en)
MX (1) MX2007012176A (en)
WO (1) WO2006105279A2 (en)

Families Citing this family (7)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US8282916B2 (en) * 2008-02-21 2012-10-09 New York University Tumor therapy with replication competent sindbis viral vectors
WO2010005704A2 (en) * 2008-06-13 2010-01-14 New York University Novel helper plasmid, defective sindbis viral vectors and methods of use thereof
EP3589312A1 (en) 2017-03-03 2020-01-08 New York University Induction and enhancement of antitumor immunity involving virus vectors expressing multiple epitopes of tumor associated antigens and immune checkpoint inhibitors or proteins
EP3762023A4 (en) 2018-03-05 2021-12-29 New York University Induction and enhancement of antitumor immunity involving sindbis virus vectors expressing immune checkpoint proteins
WO2021007276A1 (en) 2019-07-08 2021-01-14 New York University Tumor immunotherapy using sindbis viral vectors and agonist monoclonal antibodies
CN116286983A (en) * 2023-01-18 2023-06-23 中国科学院深圳先进技术研究院 SINV vector expressing IL-7 and its application in the preparation of antitumor drugs
WO2025171152A1 (en) * 2024-02-06 2025-08-14 Amplitude Therapeutics, Inc. Trans-replicating and self-replicating rnas comprising a modified 5' utr region

Family Cites Families (21)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US5091309A (en) 1986-01-16 1992-02-25 Washington University Sindbis virus vectors
US5217879A (en) 1989-01-12 1993-06-08 Washington University Infectious Sindbis virus vectors
SE9003978D0 (en) 1990-12-13 1990-12-13 Henrik Garoff DNA EXPRESSION SYSTEM BASED ON A VIRUS REPLICATION
US6770283B1 (en) 1990-12-13 2004-08-03 Bioption Ab DNA expression systems based on alphaviruses
US6015686A (en) 1993-09-15 2000-01-18 Chiron Viagene, Inc. Eukaryotic layered vector initiation systems
SE9401091D0 (en) 1994-03-31 1994-03-31 Bioption Ab Alphavirus cDNA vectors
SE9401709D0 (en) 1994-05-18 1994-05-18 Mathilda Sjoeberg Improved alphavirus vectors for expression of heterologous DNA
US6451592B1 (en) 1996-04-05 2002-09-17 Chiron Corporation Recombinant alphavirus-based vectors with reduced inhibition of cellular macromolecular synthesis
US6458560B1 (en) 1996-04-05 2002-10-01 Chiron Corporation Recombinant alphavirus-based vectors with reduced inhibition of cellular macromolecular synthesis
AU9603898A (en) 1997-10-09 1999-05-03 Pro-Virus, Inc. Treatment of neoplasms with viruses
US6197502B1 (en) * 1997-11-17 2001-03-06 Cytos Biotechnology Ag Expression cloning processes for the discovery characterization, and isolation of genes encoding polypeptides with a predetermined property
WO1999044423A1 (en) 1998-03-03 1999-09-10 The Uab Research Foundation Amplification of gene transfer and gene therapy by controlled replication
FI109847B (en) * 1998-06-11 2002-10-15 Abb Oy Procedure for minimizing the error in a synchronous motor rotor angle estimate
WO2000039318A1 (en) 1998-12-31 2000-07-06 Chiron Corporation Compositions and methods for packaging of alphavirus vectors
US6329201B1 (en) 1998-12-31 2001-12-11 Chiron Corporation Compositions and methods for packaging of alphavirus vectors
CA2370187C (en) 1999-04-15 2011-08-02 Pro-Virus, Inc. Treatment of neoplasms with viruses
US6730297B1 (en) 1999-05-28 2004-05-04 Chiron Corporation Use of recombinant gene delivery vectors for treating or preventing lysosomal storage disorders
AU7938900A (en) 1999-10-27 2001-05-08 Cytos Biotechnology Ag Method for creating divergent populations of nucleic acid molecules and proteins
WO2002044394A2 (en) * 2000-11-29 2002-06-06 University Of Southern California Targetet retoviral vectors for cancer immunotherapy
AU2002306736A1 (en) 2001-03-16 2002-10-03 Johns Hopkins University A replication-defective alphavirus vaccine linking antigen with an immunogenicity-potentiating polypeptide and a method of delivery the same
WO2002076468A1 (en) 2001-03-27 2002-10-03 New York University Tumor therapy with alphavirus-based and high affinity laminin receptor-targeted vectors

Also Published As

Publication number Publication date
MX2007012176A (en) 2007-12-13
WO2006105279A9 (en) 2007-01-25
US20080161261A1 (en) 2008-07-03
EP1871425A2 (en) 2008-01-02
CA2602730C (en) 2012-03-27
US20070020236A1 (en) 2007-01-25
US7303898B2 (en) 2007-12-04
EP1871425A4 (en) 2009-09-30
WO2006105279A3 (en) 2009-04-16
US20080300394A1 (en) 2008-12-04
EP1871425B1 (en) 2014-04-30
HK1115811A1 (en) 2008-12-12
WO2006105279A2 (en) 2006-10-05
IL186234A (en) 2012-08-30
US8530232B2 (en) 2013-09-10
AU2006230354B2 (en) 2010-10-28
US20080096837A1 (en) 2008-04-24
AU2006230354A1 (en) 2006-10-05
JP4729615B2 (en) 2011-07-20
JP2008534014A (en) 2008-08-28
IL186234A0 (en) 2008-01-20

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