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MX2019013172A - Composiciones y metodos para tratar la enfermedad de huntington. - Google Patents

Composiciones y metodos para tratar la enfermedad de huntington.

Info

Publication number
MX2019013172A
MX2019013172A MX2019013172A MX2019013172A MX2019013172A MX 2019013172 A MX2019013172 A MX 2019013172A MX 2019013172 A MX2019013172 A MX 2019013172A MX 2019013172 A MX2019013172 A MX 2019013172A MX 2019013172 A MX2019013172 A MX 2019013172A
Authority
MX
Mexico
Prior art keywords
disease
methods
compositions
treating huntington
huntington
Prior art date
Application number
MX2019013172A
Other languages
English (en)
Inventor
Xin Wang
Jinzhao Hou
Pengcheng Zhou
Dinah Wen-Yee Sah
Fen Chen
Yanquan Shu
Original Assignee
Voyager Therapeutics Inc
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Voyager Therapeutics Inc filed Critical Voyager Therapeutics Inc
Publication of MX2019013172A publication Critical patent/MX2019013172A/es

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    • C12N15/09Recombinant DNA-technology
    • C12N15/11DNA or RNA fragments; Modified forms thereof; Non-coding nucleic acids having a biological activity
    • C12N15/113Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides; Antisense DNA or RNA; Triplex- forming oligonucleotides; Catalytic nucleic acids, e.g. ribozymes; Nucleic acids used in co-suppression or gene silencing
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    • C12N2750/14011Parvoviridae
    • C12N2750/14111Dependovirus, e.g. adenoassociated viruses
    • C12N2750/14141Use of virus, viral particle or viral elements as a vector
    • C12N2750/14143Use of virus, viral particle or viral elements as a vector viral genome or elements thereof as genetic vector

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Abstract

La presente invencion se refiere a las partículas virales adeno-asociadas (AAV) que codifican moleculas de siRNA y metodos para tratar la Enfermedad de Huntington (HD).
MX2019013172A 2017-05-05 2018-05-04 Composiciones y metodos para tratar la enfermedad de huntington. MX2019013172A (es)

Applications Claiming Priority (4)

Application Number Priority Date Filing Date Title
US201762501786P 2017-05-05 2017-05-05
US201762507921P 2017-05-18 2017-05-18
US201762520086P 2017-06-15 2017-06-15
PCT/US2018/031117 WO2018204803A1 (en) 2017-05-05 2018-05-04 Compositions and methods of treating huntington's disease

Publications (1)

Publication Number Publication Date
MX2019013172A true MX2019013172A (es) 2020-09-07

Family

ID=64016307

Family Applications (1)

Application Number Title Priority Date Filing Date
MX2019013172A MX2019013172A (es) 2017-05-05 2018-05-04 Composiciones y metodos para tratar la enfermedad de huntington.

Country Status (9)

Country Link
US (2) US11752181B2 (es)
EP (1) EP3619308A4 (es)
JP (2) JP2020518259A (es)
CN (2) CN119491003A (es)
AU (2) AU2018261003A1 (es)
CA (1) CA3061368A1 (es)
MX (1) MX2019013172A (es)
SG (1) SG11201909868YA (es)
WO (1) WO2018204803A1 (es)

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