[go: up one dir, main page]

HK40070121A - New adeno-associated virus (aav) variants and uses thereof for gene therapy - Google Patents

New adeno-associated virus (aav) variants and uses thereof for gene therapy Download PDF

Info

Publication number
HK40070121A
HK40070121A HK62022059173.4A HK62022059173A HK40070121A HK 40070121 A HK40070121 A HK 40070121A HK 62022059173 A HK62022059173 A HK 62022059173A HK 40070121 A HK40070121 A HK 40070121A
Authority
HK
Hong Kong
Prior art keywords
aav
variants
gene therapy
associated virus
new adeno
Prior art date
Application number
HK62022059173.4A
Other languages
Chinese (zh)
Inventor
Jessica Zucman-Rossi
Jean-Charles NAULT
Tiziana LA BELLA
Giuseppe RONZITTI
Sandrine IMBEAUD
Patrice VIDAL
Original Assignee
INSERM (Institut National de la Santé et de la Recherche Médicale)
Assistance Publique-Hôpitaux De Paris (Aphp)
Généthon
Sorbonne Université
Université Paris Cité
Université D'evry Val D'essonne
Université Paris XIII Paris-Nord Villetaneuse
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by INSERM (Institut National de la Santé et de la Recherche Médicale), Assistance Publique-Hôpitaux De Paris (Aphp), Généthon, Sorbonne Université, Université Paris Cité, Université D'evry Val D'essonne, Université Paris XIII Paris-Nord Villetaneuse filed Critical INSERM (Institut National de la Santé et de la Recherche Médicale)
Publication of HK40070121A publication Critical patent/HK40070121A/en

Links

HK62022059173.4A 2019-04-23 2020-04-23 New adeno-associated virus (aav) variants and uses thereof for gene therapy HK40070121A (en)

Applications Claiming Priority (1)

Application Number Priority Date Filing Date Title
EP19305521.7 2019-04-23

Publications (1)

Publication Number Publication Date
HK40070121A true HK40070121A (en) 2022-10-21

Family

ID=

Similar Documents

Publication Publication Date Title
EP4041755A4 (en) Modified aav capsids and uses thereof
IL276859A (en) Novel adeno-associated virus (aav) vectors, aav vectors having reduced capsid deamidation and uses therefor
SG11202103102WA (en) Adeno-associated virus compositions for targeted gene therapy
IL276860A (en) Novel adeno-associated virus (aav) vectors, aav vectors having reduced capsid deamidation and uses therefor
EP3911354B8 (en) Aav-mediated gene therapy restoring the otoferlin gene
EP4013770A4 (en) Aav capsid variants for gene therapy
AU2019265855B2 (en) Adeno-associated virus (AAV) delivery of anti-FAM19A5 antibodies
IL291136A (en) Methods and compositions for modulating the interaction between adeno-associated virus (aav) and the aav receptor (aavr) for altered bio-distribution of aav
EP3746113A4 (en) Adeno-associated virus compositions for pah gene transfer and methods of use thereof
IL287614A (en) Modified adeno-associated virus (aav) particles for gene therapy
IL299380A (en) Improved adeno-associated virus gene therapy vectors
EP3980447A4 (en) Adeno-associated virus compositions for arsa gene transfer and methods of use thereof
IL297780A (en) Controlled modification of adeno-associated virus (aav) for enhanced gene therapy
HK40070121A (en) New adeno-associated virus (aav) variants and uses thereof for gene therapy
EP4073087A4 (en) Recombinant adeno-associated viral vector for gene delivery
HK40071702A (en) Modified adeno-associated virus (aav) particles for gene therapy
HK40095654A (en) Improved adeno-associated virus gene therapy vectors
HK40076701A (en) Aav capsid variants for gene therapy
HK40078604A (en) Adeno-associated virus (aav) systems for treatment of genetic hearing loss
HK40078892A (en) Modified aav capsids and uses thereof
HK40106241A (en) Aav for the gene therapy of wet-amd
HK40046193A (en) Adeno-associated virus (aav) delivery of anti-fam19a5 antibodies
HK40059043A (en) Recombinant adeno-associated viruses and uses thereof
HK40044076A (en) Novel adeno-associated virus (aav) vectors, aav vectors having reduced capsid deamidation and uses therefor
HK40044078A (en) Novel adeno-associated virus (aav) vectors, aav vectors having reduced capsid deamidation and uses therefor