DK3102673T3 - Fremgangsmåder og sammensætninger til behandling af beta-talassæmi - Google Patents
Fremgangsmåder og sammensætninger til behandling af beta-talassæmi Download PDFInfo
- Publication number
- DK3102673T3 DK3102673T3 DK15742584.4T DK15742584T DK3102673T3 DK 3102673 T3 DK3102673 T3 DK 3102673T3 DK 15742584 T DK15742584 T DK 15742584T DK 3102673 T3 DK3102673 T3 DK 3102673T3
- Authority
- DK
- Denmark
- Prior art keywords
- talassemi
- beta
- compositions
- treatment
- methods
- Prior art date
Links
- 239000000203 mixture Substances 0.000 title 1
Classifications
-
- C—CHEMISTRY; METALLURGY
- C07—ORGANIC CHEMISTRY
- C07K—PEPTIDES
- C07K14/00—Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof
- C07K14/795—Porphyrin- or corrin-ring-containing peptides
- C07K14/805—Haemoglobins; Myoglobins
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
- A61K35/00—Medicinal preparations containing materials or reaction products thereof with undetermined constitution
- A61K35/12—Materials from mammals; Compositions comprising non-specified tissues or cells; Compositions comprising non-embryonic stem cells; Genetically modified cells
- A61K35/28—Bone marrow; Haematopoietic stem cells; Mesenchymal stem cells of any origin, e.g. adipose-derived stem cells
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P7/00—Drugs for disorders of the blood or the extracellular fluid
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
- A61K35/00—Medicinal preparations containing materials or reaction products thereof with undetermined constitution
- A61K35/12—Materials from mammals; Compositions comprising non-specified tissues or cells; Compositions comprising non-embryonic stem cells; Genetically modified cells
- A61K2035/124—Materials from mammals; Compositions comprising non-specified tissues or cells; Compositions comprising non-embryonic stem cells; Genetically modified cells the cells being hematopoietic, bone marrow derived or blood cells
-
- C—CHEMISTRY; METALLURGY
- C07—ORGANIC CHEMISTRY
- C07K—PEPTIDES
- C07K2319/00—Fusion polypeptide
- C07K2319/80—Fusion polypeptide containing a DNA binding domain, e.g. Lacl or Tet-repressor
- C07K2319/81—Fusion polypeptide containing a DNA binding domain, e.g. Lacl or Tet-repressor containing a Zn-finger domain for DNA binding
Landscapes
- Health & Medical Sciences (AREA)
- Chemical & Material Sciences (AREA)
- Life Sciences & Earth Sciences (AREA)
- Organic Chemistry (AREA)
- Medicinal Chemistry (AREA)
- General Health & Medical Sciences (AREA)
- Immunology (AREA)
- Developmental Biology & Embryology (AREA)
- Cell Biology (AREA)
- Engineering & Computer Science (AREA)
- Hematology (AREA)
- Pharmacology & Pharmacy (AREA)
- Animal Behavior & Ethology (AREA)
- Public Health (AREA)
- Veterinary Medicine (AREA)
- Genetics & Genomics (AREA)
- Zoology (AREA)
- Biotechnology (AREA)
- Molecular Biology (AREA)
- Biochemistry (AREA)
- Biomedical Technology (AREA)
- Virology (AREA)
- Biophysics (AREA)
- Gastroenterology & Hepatology (AREA)
- Proteomics, Peptides & Aminoacids (AREA)
- Epidemiology (AREA)
- Bioinformatics & Cheminformatics (AREA)
- Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
- Diabetes (AREA)
- Chemical Kinetics & Catalysis (AREA)
- General Chemical & Material Sciences (AREA)
- Micro-Organisms Or Cultivation Processes Thereof (AREA)
- Enzymes And Modification Thereof (AREA)
- Wood Science & Technology (AREA)
- Medicines Containing Material From Animals Or Micro-Organisms (AREA)
- Acyclic And Carbocyclic Compounds In Medicinal Compositions (AREA)
- Microbiology (AREA)
- General Engineering & Computer Science (AREA)
- Separation Of Suspended Particles By Flocculating Agents (AREA)
Applications Claiming Priority (2)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201461935219P | 2014-02-03 | 2014-02-03 | |
| PCT/US2015/014103 WO2015117081A2 (en) | 2014-02-03 | 2015-02-02 | Methods and compositions for treatment of a beta thalessemia |
Publications (1)
| Publication Number | Publication Date |
|---|---|
| DK3102673T3 true DK3102673T3 (da) | 2020-07-06 |
Family
ID=53754265
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| DK15742584.4T DK3102673T3 (da) | 2014-02-03 | 2015-02-02 | Fremgangsmåder og sammensætninger til behandling af beta-talassæmi |
Country Status (12)
| Country | Link |
|---|---|
| US (1) | US10072066B2 (da) |
| EP (1) | EP3102673B1 (da) |
| DK (1) | DK3102673T3 (da) |
| ES (1) | ES2796087T3 (da) |
| HR (1) | HRP20201038T1 (da) |
| HU (1) | HUE051232T2 (da) |
| LT (1) | LT3102673T (da) |
| PL (1) | PL3102673T3 (da) |
| PT (1) | PT3102673T (da) |
| RS (1) | RS60514B1 (da) |
| SI (1) | SI3102673T1 (da) |
| WO (1) | WO2015117081A2 (da) |
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| US9388430B2 (en) | 2013-09-06 | 2016-07-12 | President And Fellows Of Harvard College | Cas9-recombinase fusion proteins and uses thereof |
| US9737604B2 (en) | 2013-09-06 | 2017-08-22 | President And Fellows Of Harvard College | Use of cationic lipids to deliver CAS9 |
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| US11053481B2 (en) | 2013-12-12 | 2021-07-06 | President And Fellows Of Harvard College | Fusions of Cas9 domains and nucleic acid-editing domains |
| AU2015298571B2 (en) | 2014-07-30 | 2020-09-03 | President And Fellows Of Harvard College | Cas9 proteins including ligand-dependent inteins |
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| KR20190127797A (ko) | 2017-03-10 | 2019-11-13 | 프레지던트 앤드 펠로우즈 오브 하바드 칼리지 | 시토신에서 구아닌으로의 염기 편집제 |
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-
2015
- 2015-02-02 US US14/611,880 patent/US10072066B2/en active Active
- 2015-02-02 PT PT157425844T patent/PT3102673T/pt unknown
- 2015-02-02 HR HRP20201038TT patent/HRP20201038T1/hr unknown
- 2015-02-02 EP EP15742584.4A patent/EP3102673B1/en active Active
- 2015-02-02 LT LTEP15742584.4T patent/LT3102673T/lt unknown
- 2015-02-02 WO PCT/US2015/014103 patent/WO2015117081A2/en not_active Ceased
- 2015-02-02 HU HUE15742584A patent/HUE051232T2/hu unknown
- 2015-02-02 RS RS20200781A patent/RS60514B1/sr unknown
- 2015-02-02 SI SI201531272T patent/SI3102673T1/sl unknown
- 2015-02-02 ES ES15742584T patent/ES2796087T3/es active Active
- 2015-02-02 DK DK15742584.4T patent/DK3102673T3/da active
- 2015-02-02 PL PL15742584T patent/PL3102673T3/pl unknown
Also Published As
| Publication number | Publication date |
|---|---|
| ES2796087T3 (es) | 2020-11-25 |
| PL3102673T3 (pl) | 2020-11-02 |
| WO2015117081A3 (en) | 2015-09-24 |
| WO2015117081A2 (en) | 2015-08-06 |
| RS60514B1 (sr) | 2020-08-31 |
| HUE051232T2 (hu) | 2021-03-01 |
| US10072066B2 (en) | 2018-09-11 |
| US20150218253A1 (en) | 2015-08-06 |
| LT3102673T (lt) | 2020-08-25 |
| EP3102673B1 (en) | 2020-04-15 |
| PT3102673T (pt) | 2020-05-21 |
| EP3102673A2 (en) | 2016-12-14 |
| SI3102673T1 (sl) | 2020-11-30 |
| HRP20201038T1 (hr) | 2020-10-16 |
| EP3102673A4 (en) | 2017-11-01 |
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