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BR0311539A - Increased release of a nucleic acid construct in vivo by the poly-l-glutamate ("plg") system - Google Patents

Increased release of a nucleic acid construct in vivo by the poly-l-glutamate ("plg") system

Info

Publication number
BR0311539A
BR0311539A BR0311539-9A BR0311539A BR0311539A BR 0311539 A BR0311539 A BR 0311539A BR 0311539 A BR0311539 A BR 0311539A BR 0311539 A BR0311539 A BR 0311539A
Authority
BR
Brazil
Prior art keywords
plg
glutamate
dna
poly
plasmid dna
Prior art date
Application number
BR0311539-9A
Other languages
Portuguese (pt)
Inventor
Ruxandra Draghia-Akli
Robert H Carpenter
Douglas R Kern
Leigh Anne Hill
Heather Attra
Henry Hebel
Original Assignee
Advisys Inc
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Priority claimed from US10/395,709 external-priority patent/US20040014645A1/en
Application filed by Advisys Inc filed Critical Advisys Inc
Publication of BR0311539A publication Critical patent/BR0311539A/en

Links

Classifications

    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61KPREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K48/00Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy
    • A61K48/0008Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy characterised by an aspect of the 'non-active' part of the composition delivered, e.g. wherein such 'non-active' part is not delivered simultaneously with the 'active' part of the composition
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61KPREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K48/00Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy

Landscapes

  • Health & Medical Sciences (AREA)
  • Life Sciences & Earth Sciences (AREA)
  • Chemical & Material Sciences (AREA)
  • Engineering & Computer Science (AREA)
  • Biotechnology (AREA)
  • Genetics & Genomics (AREA)
  • Medicinal Chemistry (AREA)
  • Molecular Biology (AREA)
  • Pharmacology & Pharmacy (AREA)
  • Epidemiology (AREA)
  • Animal Behavior & Ethology (AREA)
  • General Health & Medical Sciences (AREA)
  • Public Health (AREA)
  • Veterinary Medicine (AREA)
  • Micro-Organisms Or Cultivation Processes Thereof (AREA)
  • Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
  • Peptides Or Proteins (AREA)

Abstract

"LIBERAçãO AUMENTADA DE UM CONSTRUCTO DE áCIDO NUCLéICO IN VIVO PELO SISTEMA DE POLI-L-GLUTAMATO ('PLG')". DNA plasmídeo liberado por injeção / eletroporação para o músculo do esqueleto pode ser expresso, e níveis fisiológicos de transgene podem ser obtidos na circulação. Não obstante, estabilização de DNA nu pode ser requerida e necessária em alguns casos, como estocagem prolongada em diferentes temperaturas antes de utilização, injeção em um grande número de animais, etc. é imperativo que o composto associado não seja tóxico para as células (por exemplo, células de músculo) ou cause ruptura de DNA plasmídeo. Pode ser preferível para o DNA revestido ter uma tomada similar ou aumentada nas células alvo. Compostos poli-L-glutamato de baixo peso molecular têm todas as propriedades desejadas. Foi determinado que a razão mol / mol de DNA/PLG é a concentração ótima para aplicações terapêuticas de gene para o músculo de esqueleto, resultando em aumentada expressão do transgene, sem dano para o tecido alvo. Além disso, estabilização de DNA plasmídeo por PLG nunca foi observada ou descrita na literatura."INCREASED RELEASE OF IN VIVO NUCLEIC ACID CONSTRUCTION BY THE POLY-L-GLUTAMATE ('PLG') SYSTEM". Plasmid DNA released by injection / electroporation into the skeletal muscle can be expressed, and physiological levels of transgene can be obtained in the circulation. However, bare DNA stabilization may be required and necessary in some cases, such as prolonged storage at different temperatures before use, injection into a large number of animals, etc. It is imperative that the associated compound be non-toxic to cells (e.g., muscle cells) or cause plasmid DNA disruption. It may be preferable for the coated DNA to have a similar or increased uptake in the target cells. Low molecular weight poly-L-glutamate compounds have all the desired properties. It has been determined that the mol / mol ratio of DNA / PLG is the optimal concentration for therapeutic gene applications for skeletal muscle, resulting in increased transgene expression without damage to the target tissue. Moreover, plasmid DNA stabilization by PLG has never been observed or described in the literature.

BR0311539-9A 2002-05-28 2003-05-23 Increased release of a nucleic acid construct in vivo by the poly-l-glutamate ("plg") system BR0311539A (en)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US15667002A 2002-05-28 2002-05-28
US10/395,709 US20040014645A1 (en) 2002-05-28 2003-03-24 Increased delivery of a nucleic acid construct in vivo by the poly-L-glutamate ("PLG") system
PCT/US2003/016541 WO2003099341A1 (en) 2002-05-28 2003-05-23 Increased delivery of a nucleic acid constrtuct in vivo by the poly-l-glutamate (plg) system

Publications (1)

Publication Number Publication Date
BR0311539A true BR0311539A (en) 2005-10-25

Family

ID=29586320

Family Applications (1)

Application Number Title Priority Date Filing Date
BR0311539-9A BR0311539A (en) 2002-05-28 2003-05-23 Increased release of a nucleic acid construct in vivo by the poly-l-glutamate ("plg") system

Country Status (7)

Country Link
EP (1) EP1513559A4 (en)
CN (1) CN1662261A (en)
AU (1) AU2003273142A1 (en)
BR (1) BR0311539A (en)
CA (1) CA2485976A1 (en)
MX (1) MXPA04011766A (en)
WO (1) WO2003099341A1 (en)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
JPWO2005089810A1 (en) * 2004-03-22 2008-01-31 関西ティー・エル・オー株式会社 Bone induction method by introducing human bone morphogenetic gene using electroporation method
US20060025368A1 (en) * 2004-07-23 2006-02-02 Advisys, Inc. Growth hormone releasing hormone enhances vaccination response

Family Cites Families (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
ATE309358T1 (en) * 1999-07-26 2005-11-15 Baylor College Medicine SUPERACTIVE GROWTH HORMONE RELEASING HORMONE ANALOGUES FROM PORK
CA2401327C (en) * 2000-03-03 2014-05-06 Valentis, Inc. Nucleic acid formulations comprising poly-amino acids for gene delivery and methods of use
BR0214869A (en) * 2001-12-11 2005-03-08 Advisys Inc Plasmid-mediated supplementation for treatment of chronically ill individuals

Also Published As

Publication number Publication date
WO2003099341A1 (en) 2003-12-04
CN1662261A (en) 2005-08-31
CA2485976A1 (en) 2003-12-04
EP1513559A1 (en) 2005-03-16
AU2003273142A1 (en) 2003-12-12
EP1513559A4 (en) 2006-01-18
MXPA04011766A (en) 2005-03-31

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Legal Events

Date Code Title Description
B11A Dismissal acc. art.33 of ipl - examination not requested within 36 months of filing
B11Y Definitive dismissal - extension of time limit for request of examination expired [chapter 11.1.1 patent gazette]